Preclinical Development of Antisense Oligonucleotides to Rescue Aberrant Splicing Caused by an Ultrarare <i>ABCA4</i> Variant in a Child with Early-Onset Stargardt Disease

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Publication year
2024
Author(s)
Suárez Herrera, N.
Li, C.H.Z.
Leijsten, Nico
Karjosukarso, D.W.
Corradi, Z.
Bukkems, F.
Duijkers, L.E.M.
Cremers, F.P.M.
Hoyng, C.B.
Garanto, A.
Collin, R.W.J.
Source
Cells, 13, 7, (2024), article 601
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Publication type
Article / Letter to editor
Please use this identifier to cite or link to this item: https://hdl.handle.net/2066/305681   https://hdl.handle.net/2066/305681
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